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Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and...

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Trusted evidence. Informed decisions. Better health. Trusted evidence. Informed decisions. Better health. Trusted evidence. Informed decisions. Better health. Benchmarking Controlled Trial - a novel concept covering all observational effectiveness studies Antti Malmivaara, MD, PhD, Chief Physician Centre for Health and Social Economics National Institute for Health and Welfare Helsinki, Finland
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Page 1: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Trusted evidence. Informed decisions. Better health.

Trusted evidence. Informed decisions. Better health.

Trusted evidence. Informed decisions. Better health.

Benchmarking Controlled

Trial - a novel concept

covering all observational

effectiveness studies

Antti Malmivaara, MD, PhD, Chief Physician

Centre for Health and Social Economics

National Institute for Health and Welfare

Helsinki, Finland

Page 2: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Potential conflicts of interests

Finnish Institute for Health and Welfare, Centre for Health and

Social Economics, Chief Physician

Current Care Guidelines, Finnish Medical Association

Duodecim, Editor

Ministry for Social Affairs and Health, Council for Choices in

Health care in Finland, Expert

Hospital ORTON, Scientific Board, Member

European Academy of Rehabilitation Medicine

Cochrane Back and Neck Review Group, Editorial Board

Cochrane Rehabilitation Field, Executive Committee; Chair of

the Methodology Committee

Antti Malmivaara, Käypä hoito/Duodecim, CHESS/THL

Page 3: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific
Page 4: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Real-Effectiveness Medicine

Malmivaara A. Real-Effectiveness Medicine – pursuing the best effectiveness in the ordinary

care of patients. Annals of Medicine 2013;45:103-106.

Randomized

controlled

trials

Benchmarking

controlled trials

Page 5: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Malmivaara A. Benchmarking Controlled Trial – a novel concept covering all observational

effectiveness studies.. Annals of Medicine 2015;47:332-40.

Page 6: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Malmivaara A. Benchmarking Controlled Trial – a novel concept covering all observational

effectiveness studies.. Annals of Medicine 2015;47:332-40.

Page 7: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific
Page 8: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Malmivaara A. Clinical Impact Research. Annals of Medicine 2016;Aug 5:1-4

Page 9: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific
Page 10: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

EuroHOPE-project. One year mortality for

ischaemic stroke in six countries.

Malmivaara A, Meretoja A, Peltola et al. Comparing ischaemic stroke in six European countries. The EuroHOPE

register study. Eur J Neurol, 2015;22:221–418

Antti Malmivaara, Terveys- ja sosiaalitalous -yksikkö, THL

Page 11: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific
Page 12: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Malmivaara A. System Impact Research – increasing public health and health care system performance. Annals of

Medicine 2016;March 15:1-5

Page 13: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Four year follow-up study of

memory disorder patients in

Helsinki and Espoo

Rosenvall A, Rättö H, Finne-Soveri H, Häkkinen U, Juntunen M, Järvelin

J, Linnosmaa I, Noro A, Kuronen M, Malmivaara A. Neljän vuoden

seurantatutkimus helsinkiläisistä ja espoolaisista muistisairaista:

palvelujen käyttö, pitkäaikaishoito ja kuolleisuus. Suomen Lääkärilehti

2015;70:2332-2339

Page 14: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Rosenvall A ym. Neljän vuoden seurantatutkimus helsinkiläisistä ja espoolaisista muistisairaista: palvelujen

käyttö, pitkäaikaishoito ja kuolleisuus. Suomen Lääkärilehti 2015;70:2332-2339

Page 15: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Rosenvall A ym. Neljän vuoden seurantatutkimus helsinkiläisistä ja espoolaisista muistisairaista: palvelujen

käyttö, pitkäaikaishoito ja kuolleisuus. Suomen Lääkärilehti 2015;70:2332-2339

Page 16: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Potential cost savings of selected non-

pharmacological treatment strategies for

Alzheimer’s disease in Finland - a cost-

neutrality model (Manuscript)

Ari Rosenvall, Lauri Sääksvuori, Harriet Finne-Soveri, Ismo Linnosmaa,

Antti Malmivaara

Page 17: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Cost savings due to care management,

family support and rehabilitation

Page 18: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Conclusions

Page 19: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Benchmarking Controlled Trial (BCT)

Benchmarking Controlled Trial (BCT) is a new

concept which covers all observational effectiveness

studies.

BCTs are capable of assessing clinical effectiveness

and effects of features of the health and social care

system.

Study design is based on benchmarking between

health care providers taking care of similar patient or

population groups.

Malmivaara A. Benchmarking Controlled Trial – a novel concept covering all observational effectiveness

studies. Annals of Medicine 2015;47:332-40.

Page 20: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific
Page 21: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific
Page 22: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

The four stages in pursuing scientific

evidence of effectiveness in rehabilitation

1. Decide upon the most relevant study question(s)

2. Decide whether RCT or BCT is the study design

of choice

3. Pursue the best possible internal and external

validity (generalizability of results) when planning

and conducting the study

4. Report according to current guidelines

Page 23: Benchmarking Controlled Trial - a novel concept covering all ......Ministry for Social Affairs and Health, Council for Choices in Health care in Finland, Expert Hospital ORTON, Scientific

Trusted evidence. Informed decisions. Better health.

Trusted evidence. Informed decisions. Better health.

Trusted evidence. Informed decisions. Better health.

Thank you!


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