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Hematology/Oncology Department at UCSF Benioff
Children's Hospital Oakland
Recent Faculty Publications (2012 -2015)
Books:
Agrawal AK, Hastings C, Feusner J, eds. Supportive Care in
Pediatric Oncology. Berlin: Springer; 2015.
https://books.google.com/books?id=dSB2oAEACAAJ.
Hastings CA, Torkildson JC, Agrawal AK. Handbook of Pediatric
Hematology and Oncology: Children's Hospital and Research
Center Oakland. Second ed. West Sussex, United Kingdom: John
Wiley & Sons, Ltd.; 2012. http://www.amazon.com/Handbook-
Pediatric-Hematology-Oncology-Childrens/dp/0470670886.
Taher A, Vichinsky E, Musallam K, Cappellini MD, Viprakasit V. Guidelines for the Management
of Non Tranfusion Dependent Thalassemia (NTDT). ed. Cyprus: Thalassemia International
Federation; 2013. http://thalassemia.com/documents/NTDT-TIF-guidelines.pdf.
Vichinsky E, Levine L, Bhatia S, Bojanowski J, Coates T, Foote D, Fung E, Harmatz P, Jeng M,
Knudsen J, Lal A, Pakbaz Z, Schroepfer C, Singer ST, Sweeters N, Walters M, Wood J.
Standards of Care Guidelines for Thalassemia. Oakland, California: Children's Hospital &
Research Center Oakland; 2012.
http://hemonc.cho.org/thalassemia/documents/SOCGuidelines2012.pdf.
Vichinsky E, ed. Emerging Therapies Targeting the Pathophysiology of Sickle Cell Disease.
Hematology/Oncology Cinics of North America 2014/03/05 ed. Philadelphia, PA: Elsevier, Inc.;
2014. http://www.sciencedirect.com/science/journal/08898588/28/2.
Book Chapters:
Agrawal AK. Immunization Practice in Pediatric Oncology. In: Agrawal AK, Hastings CH,
Feusner J, eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach. Berlin:
Springer; 2015.
Agrawal AK, Feusner J. Supportive Care of Patients with Cancer. In: Lanzkowsky P, Lipton
JM, Fish JD, eds. Manual of Pediatric Hematology and Oncology. 6th ed: Springer; 2015 (in press).
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Agrawal AK, Hastings C, Feusner J.
Knowledge Gaps and Opportunities for
Research. In: Agrawal AK, Hastings CH,
Feusner J, eds. Supportive Care in Pediatric
Oncology: A Practical Evidence-Based
Approach. Berlin: Springer; 2015.
Agrawal AK, Hord JD. Hematopoietic
Growth Factors. In: Agrawal AK, Hastings
CH, Feusner J, eds. Supportive Care in
Pediatric Oncology: A Practical Evidence-Based Approach. Berlin: Springer; 2015.
Agrawal AK, Shah SS. Pediatrics. In: Gulati A, Puttanniah V, Byas-Smith M, eds. Essentials of
Interventional Cancer Pain Management. New York: Springer; 2015 (in press).
Aguilar A, Agrawal AK, Feusner J. Hyperleukocytosis. In: Agrawal AK, Hastings CH, Feusner J,
eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach. Berlin: Springer;
2015.
Ataga K, Vichinsky E. Thrombotic complications in sickle cell disease. In: Marder VJ, Aird WC,
Bennett JS, Schulman S, White GC, eds. Hemostasis and Thrombosis: Basic Principles and Clinical
Practice. Chapter 122, Sixth (November 2012) ed. Philadelphia, PA: Lippincott Williams &
Wilkins; 2012:p. 1445. http://books.google.com/books?
id=_SVbYgEACAAJ&dq=9781608319060.
Chung JH, Agrawal AK, Swift PS. Acute Radiation Side Effects. In: Feusner J, Hastings CA,
Agrawal AK, eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach.
Berlin: Springer; 2015.
DeBaun M, Vichinsky E. Acute pain management in adults with sickle cell disease. In: Basow
DS, ed. UpToDate. Topic 7144 Version 14.0; Oct, 2014. Waltham, MA: UpToDate, Inc.; 2014.
http://www.uptodate.com/contents/acute-pain-management-in-adults-with-sickle-cell-
disease.
DeBaun M, Vichinsky E. Red blood cell transfusion in sickle cell disease. In: Basow DS, ed.
UpToDate. Topic 90145 Version 8.0; Nov 11, 2014. Waltham, MA: UpToDate, Inc.; 2014.
http://www.uptodate.com/contents/red-blood-cell-transfusion-in-sickle-cell-disease.
DeBaun MR, Frei-Jones M, Vichinsky E. Sickle Cell Disease. In: Kliegman R, Stanton BF, St.
Geme J, Schor N, Behrman, eds. Nelson Textbook of Pediatrics, Twentieth Edition. 462.1:
Elsevier, Inc.; 2015 (in press).
Field J, Vichinsky E, DeBaun M. Overview of the management and prognosis of sickle cell
disease. In: Basow DS, ed. UpToDate. Topic 7114 Version 37.0; Dec 01, 2014. Waltham, MD:
UpToDate, Inc.; 2014. http://www.uptodate.com/contents/overview-of-the-management-of-
sickle-cell-disease.
Fung EB, Chung J. Nutrition for Children with Sickle Cell Disease and Thalassemia. In:
Kleinman RE, Greer FR, eds. Pediatric Nutrition Handbook. 7th ed. Elk Grove Village, IL: American
Academy of Pediatrics; 2014:979-92. http://reader.aappublications.org/pediatric-nutrition-7th-
edition-sponsored-member-benefit/2.
Garcia JR, Walters MC. Hematopoietic Cell Transplantation for non-malignant disorders. In:
Greer J, 13th ed., ed. Wintrobe's Clinical Hematology. Philadelphia, PA: Wolwers Kluwer /
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Lippincott Williams & Wilkins; 2014.
Gomez E, Agrawal AK, Hastings C. Transfusion Support. In: Agrawal AK, Hastings CH, Feusner
J, eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach. Berlin:
Springer; 2015.
Khurana M, Su W. The Acute Abdomen. In: Feusner J, Hastings CA, Agrawal AK, eds.
Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach. Berlin: Springer;
2015.
Lalefar NR, Lubin B. Sibling Donor Cord Blood Program: Children�s Hospital Research
Center Oakland and Beyond. In: Dusko I, ed. Stem Cell Banking. New York, NY: Humana
Press/Springer Science; 2014. http://www.amazon.com/Stem-Banking-Biology-Regenerative-
Medicine/dp/1493905848.
Lo CY, Morris CR. Vasculopathy, Chronic Oxidative Stress and Endothelial Dysfunction in
SCD. In: Acu�a-Castroviejo D, Rusanova I, eds. Sickle Cell Disease: A New Vision for an Old
Problem. Recent Advances in Hematology Research. Chapter 5; : Nova Science Publishers;
2013. https://www.novapublishers.co m/catalog/product_info.php?products_id=41344.
Marsh A, Agrawal AK, Feusner J. Tumor Lysis Syndrome. In: Agrawal AK, Hastings CH,
Feusner J, eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach.
Chapter 3. Berlin: Springer; 2015.
Marsh A, Matsunaga A. Neonatal Alloimmune Thrombocytopenia. In: Cabana MD, ed. The 5-
Minute Pediatric Consult. 7th ed: Lippincott Williams & Wilkins; 2014 (in press).
Marsh A, Vichinsky E. Sickle cell disease. In: Hoffbrand H, Higgs D, Keeling D, Mehta A, eds.
Post Graduate Haematology, 7th edition. Wiley; 2015 (in press).
Morris CR. Arginine and Asthma. In: Makrides M, Ochoa JB, Szajewska H, eds. The Importance
of Immunonutrition. Nestl� Nutrition Institute Workshop Series. Basel, Switzerland: Karger
AG; 2013: pp 1-15 (DOI:0.1159/000351365). http://www.karger.com/Article/Abstract/351365.
Morris CR, Gladwin MT. Pulmonary hypertension in sickle cell disease and thalassemia. In:
Naeije R, Rubin D, eds. Pulmonary Circulation. 4th ed. London, U.K.: Hodder Arnold; 2015 (in
press).
Quirolo K, Vichinsky E. Sickle cell anemia, thalassemia, and other inherited hemolytic
anemia In: Simon TL, McCullough J, Snyder E, Solheim BG, Strauss RG, eds. Rossi's Principles of
Transfusion Medicine, 5th edition. Wiley; 2015 (in process).
Saunthararajah Y, Vichinsky E. Sickle Cell Disease: Clinical Features and Management. In:
Hoffman R, ed. Hematology: Basic Principles and Practice. Chapter 40, 6th ed. Philadelphia, PA:
Saunders/Elsevier; 2013. http://uclibs.org/PID/62059
Vichinsky E. Overview of the clinical manifestations of sickle cell disease. In: Basow DS, ed.
UpToDate. Topic 7119 Version 27.0; Nov. 24, 2014. Waltham, MA: UpToDate, Inc.; 2014.
http://www.uptodate.com/contents/overview-of-the-clinical-manifestations-of-sickle-cell-
disease.
Vichinsky E. Pregnancy in women with sickle cell disease. In: Basow DS, ed. UpToDate. Topic
7139 Version 18.0; Sep 30, 2014. Waltham, MA: UpToDate, Inc.; 2014.
http://www.uptodate.com/contents/pregnancy-in-women-with-sickle-cell-disease.
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Vichinsky E. Sickle Cell Syndromes. In: Decision Support in Medicine.
http://decisionsupportinmedicine.com; 2013 (in process).
Vichinsky E. Sickle Cell Trait. In: Basow DS, ed. UpToDate. Topic 7145 Version 24.0; Nov 21
2014. www.UpToDate.com: UpToDate, Inc.; 2014. http://www.uptodate.com/contents/sickle-
cell-trait.
Vichinsky E. Variant Sickle Cell Syndromes. In: Basow DS, ed. UpToDate. Topic 7115 Version
11.0; March 28, 2014. Waltham, MA: UpToDate, Inc.; 2014.
http://www.uptodate.com/contents/variant-sickle-cell-syndromes.
Vichinsky E, Mahoney DH. Diagnosis of sickle cell disorders. In: Basow DS, ed. UpToDate.
Topic 7113 Version 15.0; Aug 28, 2014. Waltham, MA: UpToDate, Inc.; 2014.
http://www.uptodate.com/contents/diagnosis-of-sickle-cell-syndromes.
Walters MC. Hematopoietic cell transplantation for sickle cell disease. In: Forman SJ, Negris
RS, Antin J, Applebaum FR, eds. Hematopoietic Cell Transplantation. Fifth ed. Malden, MA:
Blackwell Science; 2014 (in press).
Journal Articles:
Adam SS, Hoppe C. Potential role for statins in sickle cell disease. Pediatr Blood Cancer
2013;60 4:60;4 p.550-7. http://www.ncbi.nlm.nih.gov/pubmed/23281161.
Afshar M, Birnbaum D, Golden C. Review of dextromethorphan administration in 18 patients
with subacute methotrexate central nervous system toxicity. Pediatr Neurol 2014;50 6:625-
9. http://www.ncbi.nlm.nih.gov/pubmed/24742799.
Afshar M, Golden C. Report of neuroblastoma in a set of monozygotic monochorionic twins.
Pediatr Hematol Oncol 2013;30 4:285-7. http://www.ncbi.nlm.nih.gov/pubmed/23373760.
Afzal SY, Wender AR, Jones MD, Fung EB, Pico EL. The effect of low magnitude mechanical
stimulation (LMMS) on bone density in patients with Rett syndrome: a pilot and feasibility
study. J Pediatr Rehabil Med 2014;7 2:167-78. http://www.ncbi.nlm.nih.gov/pubmed/25096869.
Agrawal AK, Hsu E, Quirolo K, Neumayr LD, Flori HR. Red blood cell transfusion in pediatric
patients with severe chronic anemia: how slow is necessary? Pediatr Blood Cancer 2012;58
3:466-8. http://www.ncbi.nlm.nih.gov/pubmed/21793178.
Agrawal AK, Kammen BF, Guo H, Donthineni R. An unusual presentation of subcutaneous
granuloma annulare in association with juvenile-onset diabetes: case report and literature
review. Pediatr Dermatol 2012;29 2:202-5. http://www.ncbi.nlm.nih.gov/pubmed/22085091.
Aguilar A, Saba JD. Truth and consequences of sphingosine-1-phosphate lyase. Adv Biol
Regul 2012;52 1:17-30. http://www.ncbi.nlm.nih.gov/pubmed/21946005.
Amstrong D, Neumayr L, Gold JI, Weiner MW, Rule RR, LeBeau P, Kesler K, McMahon L, Orringer
EP, Harrington T, DeCastro LM, Kalinyak K, Kutlar A, Rutherford CJ, Johnson C, Bessman JD,
Hussein A, Vichinsky E. Biologic predictors of memory, attention, and executive function in
neurologically asymptomatic adults with sickle cell anemia. 2014 (submitted).
Anglemyer A, Agrawal AK, Rutherford GW. Treatment of Kaposi sarcoma in children with
HIV-1 infection. Cochrane Database Syst Rev 2014;1:CD009826.
http://www.ncbi.nlm.nih.gov/pubmed/24464843.
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Bae HT, Baldwin CT, Sebastiani P, Telen MJ, Ashley-Koch A, Garrett M, Hooper WC, Bean CJ,
Debaun MR, Arking DE, Bhatnagar P, Casella JF, Keefer JR, Barron-Casella E, Gordeuk V, Kato
GJ, Minniti C, Taylor J, Campbell A, Luchtman-Jones L, Hoppe C, Gladwin MT, Zhang Y,
Steinberg MH. Meta-analysis of 2040 sickle cell anemia patients: BCL11A and HBS1L-MYB
are the major modifiers of HbF in African Americans. Blood 2012;120 9:1961-2.
http://www.ncbi.nlm.nih.gov/pubmed/22936743.
Ballas SK, Kesen MR, Goldberg MF, Lutty GA, Dampier C, Osunkwo I, Wang WC, Hoppe C,
Hagar W, Darbari DS, Malik P. Beyond the definitions of the phenotypic complications of
sickle cell disease: an update on management. ScientificWorldJournal 2012;2012:949535.
http://www.ncbi.nlm.nih.gov/pubmed/22924029.
Ballas SK, Kesen MR, Goldberg MF, Lutty GA, Dampier C, Osunkwo I, Wang WC, Hoppe C,
Hagar W, Darbari DS, Malik P. Erratum to "Beyond the Definitions of the Phenotypic
Complications of Sickle Cell Disease: An Update on Management". ScientificWorldJournal
2013;2013:861251. http://www.ncbi.nlm.nih.gov/pubmed/23483854.
Ballas SK, Vichinsky E. Is the Medical Home for Adult Patients with Sickle Cell Disease a
Reality or An Illusion? . Hemoglobin 2015 (in press).
Behera RK, Theil EC. Moving Fe2+ from ferritin ion channels to catalytic OH centers
depends on conserved protein cage carboxylates. Proc Natl Acad Sci U S A 2014;111
22:7925-30. http://www.ncbi.nlm.nih.gov/pubmed/24843174.
Bloch EM, Herwaldt BL, Leiby DA, Shaieb A, Herron RM, Chervenak M, Reed W, Hunter R, Ryals
R, Hagar W, Xayavong MV, Slemenda SB, Pieniazek NJ, Wilkins PP, Kjemtrup AM. The third
described case of transfusion-transmitted Babesia duncani. Transfusion 2012;52 7:1517-22.
http://www.ncbi.nlm.nih.gov/pubmed/22168221.
Chen Q, Fabry ME, Rybicki AC, Suzuka SM, Balazs TC, Etzion Z, de Jong K, Akoto EK, Canterino
JE, Kaul DK, Kuypers FA, Lefer D, Bouhassira EE, Hirsch RE. A transgenic mouse model
expressing exclusively human hemoglobin E: indications of a mild oxidative stress. Blood
Cells Mol Dis 2012;48 2:91-101. http://www.ncbi.nlm.nih.gov/pubmed/22260787.
Chokkalingam AP, Metayer C, Scelo G, Chang JS, Schiffman J, Urayama KY, Ma X, Hansen HM,
Feusner JH, Barcellos LF, Wiencke JK, Wiemels JL, Buffler PA. Fetal growth and body size
genes and risk of childhood acute lymphoblastic leukemia. Cancer Causes Control 2012;23
9:1577-85. http://www.ncbi.nlm.nih.gov/pubmed/22878902.
Cooper TM, Franklin J, Gerbing RB, Alonzo TA, Hurwitz C, Raimondi SC, Hirsch B, Smith FO,
Mathew P, Arceci RJ, Feusner J, Iannone R, Lavey RS, Meshinchi S, Gamis A. AAML03P1, a
pilot study of the safety of gemtuzumab ozogamicin in combination with chemotherapy for
newly diagnosed childhood acute myeloid leukemia: a report from the Children's Oncology
Group. Cancer 2012;118 3:761-9. http://www.ncbi.nlm.nih.gov/pubmed/21766293.
Cui J, Azimi M, Adekile AD, Al Awadhi H, Hoppe CC. Detection of anti-Lepore Hb P-Nilotic by
multiplex ligation-dependent probe amplification. Hemoglobin 2012;36 3:276-82.
http://www.ncbi.nlm.nih.gov/pubmed/22384950.
Cui J, Azimi M, Baysdorfer C, Vichinsky E, Hoppe CC. Application of multiplex ligation-
dependent probe amplification to screen for beta-globin cluster deletions: detection of two
novel deletions in a multi ethnic population. Hemoglobin 2013;37 3:241-56.
http://www.ncbi.nlm.nih.gov/pubmed/23577918.
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Cui J, Azimi M, Hoppe CC. Detection of a novel betadelta-globin fusion gene, anti-lepore Hb
CHORI (beta(through IVS-I-57)/delta(from IVS-I-101)), by multiplex ligation-
dependent probe amplification. Hemoglobin 2014;38 1:60-3.
http://www.ncbi.nlm.nih.gov/pubmed/24102354.
Cui J, Baysdorfer C, Azimi M, Vichinsky E, Hoppe CC. Identification of three novel Hb F
variants: Hb F-Hayward [Ggamma1(NA1)Gly-->Asp, GGT>GAT], Hb F-Chori-I
[AgammaT16(A13)Gly-->Asp, GGC>GAC] and Hb F-Chori-II [AgammaI29(B11)Gly--
>Glu, GGA>GAA]. Hemoglobin 2012;36 3:305-9.
http://www.ncbi.nlm.nih.gov/pubmed/22384921.
Dagri JN, Evans A, Torkildson JC, Portnow J, Ashby LS, Zakotnik B, Brown RJ, Dhall G, Finlay JL.
Feasibility of an Attenuated Maintenance chemotherapy Regimen Directed at Adolescents
and Young Adults with Newly Diagnosed Localized Medulloblastoma and Other Central
Nervous System Embryonal Tumors. J Adolescent and Young Adult Oncology 2014;3 3:106-11.
Dang DN, Morris HD, Feusner JH, Koduru P, Wilson K, Timmons CF, Cavalier M, Luu HS.
Therapy-induced Secondary Acute Myeloid Leukemia With t(11;19)(q23;p13.1) in a
Pediatric Patient With Relapsed Acute Promyelocytic Leukemia. J Pediatr Hematol Oncol
2014;36 8:e546-8. http://www.ncbi.nlm.nih.gov/pubmed/24942021.
Day LL, Murray E, Treadwell MJ, Lubin BH. Teaching about Genetics and Sickle Cell Disease
in Fifth Grade. Journal of the National Medical Association 2015 (in press).
DeBaun MR, Armstrong FD, McKinstry RC, Ware RE, Vichinsky E, Kirkham FJ. Silent cerebral
infarcts: a review on a prevalent and progressive cause of neurologic injury in sickle cell
anemia. Blood 2012;119 20:4587-96. http://www.ncbi.nlm.nih.gov/pubmed/22354000.
Delgado EM, Cho CS, Gildengorin G, Leibovich SA, Morris CR. Parental Asthma Education and
Risks for Nonadherence to Pediatric Asthma Treatments. Pediatr Emerg Care 2014;30
11:782-7 10.1097/PEC.0000000000000259. http://journals.lww.com/pec-
online/Fulltext/2014/11000/Parental_Asthma_Education_and_Risks_for.3.aspx
Derderian SC, Jeanty C, Walters MC, Vichinsky E, MacKenzie TC. In utero hematopoietic cell
transplantation for hemoglobinopathies. Front Pharmacol 2014;5:278.
http://www.ncbi.nlm.nih.gov/pubmed/25628564.
Doh I, Lee WC, Cho YH, Pisano AP, Kuypers FA. Deformation measurement of individual cells
in large populations using a single-cell microchamber array chip. Appl Phys Lett 2012;100
17:173702-1737023. http://www.ncbi.nlm.nih.gov/pubmed/22586355.
Douer D, Zickl LN, Schiffer CA, Appelbaum FR, Feusner JH, Shepherd L, Willman CL, Bloomfield
CD, Paietta E, Gallagher RE, Park JH, Rowe JM, Wiernik PH, Tallman MS. All-trans retinoic acid
and late relapses in acute promyelocytic leukemia: Very long-term follow-up of the North
American Intergroup Study I0129. Leuk Res 2013.
http://www.ncbi.nlm.nih.gov/pubmed/23528262.
Dror DK, King JC, Durand DJ, Fung EB, Allen LH. Feto-maternal vitamin D status and infant
whole-body bone mineral content in the first weeks of life. Eur J Clin Nutr 2012;66 9:1016-
9. http://www.ncbi.nlm.nih.gov/pubmed/22781021.
Dror DK, King JC, Fung EB, Van Loan MD, Gertz ER, Allen LH. Evidence of associations
between feto-maternal vitamin D status, cord parathyroid hormone and bone-specific
alkaline phosphatase, and newborn whole body bone mineral content. Nutrients 2012;4
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2:68-77. http://www.ncbi.nlm.nih.gov/pubmed/22413062.
Fens MH, Larkin SK, Oronsky B, Scicinski J, Morris CR, Kuypers FA. The capacity of red blood
cells to reduce nitrite determines nitric oxide generation under hypoxic conditions. PLoS
One 2014;9 7:e101626. http://www.ncbi.nlm.nih.gov/pubmed/25007272.
Flanagan JM, Sheehan V, Linder H, Howard TA, Wang YD, Hoppe CC, Aygun B, Adams RJ, Neale
GA, Ware RE. Genetic mapping and exome sequencing identify two mutations associated
with stroke protection in pediatric patients with sickle cell anemia. Blood 2013.
http://www.ncbi.nlm.nih.gov/pubmed/23422753.
Fung EB, Gariepy CA, Sawyer AJ, Higa A, Vichinsky E. The effect of whole body vibration
therapy on bone density in patients with thalassemia: a pilot study. Am J Hematol 2012;87
10:E76-9. http://www.ncbi.nlm.nih.gov/pubmed/22886910.
Fung EB, Kwiatkowski JL, Huang JN, Gildengorin G, King JC, Vichinsky E. Zinc supplementation
improves bone density in patients with thalassemia: a double-blind, randomized, placebo-
controlled trial. Am J Clin Nutr 2013;98 4:960-71.
http://www.ncbi.nlm.nih.gov/pubmed/23945720.
Fung EB, Xu Y, Trachtenberg F, Odame I, Kwiatkowski JL, Neufeld EJ, Thompson AA, Boudreaux
J, Quinn CT, Vichinsky E, Thalassemia Clinical Research N. Inadequate dietary intake in
patients with thalassemia. J Acad Nutr Diet 2012;112 7:980-90.
http://www.ncbi.nlm.nih.gov/pubmed/22551675.
Gallagher RE, Moser BK, Racevskis J, Poire X, Bloomfield CD, Carroll AJ, Ketterling RP, Roulston
D, Schachter-Tokarz E, Zhou DC, Chen IM, Harvey R, Koval G, Sher DA, Feusner JH, Tallman MS,
Larson RA, Powell BL, Appelbaum FR, Paietta E, Willman CL, Stock W. Treatment-influenced
associations of PML-RARalpha mutations, FLT3 mutations, and additional chromosome
abnormalities in relapsed acute promyelocytic leukemia. Blood 2012;120 10:2098-108.
http://www.ncbi.nlm.nih.gov/pubmed/22734072.
Garcia JR, Pollard J, Thomson B. Minimal Residual Disease in Acute Leukemias: review of
literature and introduction of �bridging therapy� prior to hematopoietic cell
transplantation. 2014 (submitted).
Gardner K, Hoppe C, Mijovic A, Vichinsky E, Thein SL. How we treat delayed hemolytic
transfusion reactions in patients with sickle cell disease. 2015 (in process).
Gladwin MT, Barst RJ, Gibbs JS, Hildesheim M, Sachdev V, Nouraie M, Hassell KL, Little JA,
Schraufnagel DE, Krishnamurti L, Novelli E, Girgis RE, Morris CR, Berman Rosenzweig E,
Badesch DB, Lanzkron S, Castro OL, Taylor JGt, Goldsmith JC, Kato GJ, Gordeuk VR, Machado
RF, Walk Phaast investigators. Risk factors for death in 632 patients with sickle cell
disease in the United States and United Kingdom. PloS one. 2014;9(7):e99489. Epub
2014/07/06. doi: 10.1371/journal.pone.0099489. PubMed PMID: 24988120; PubMed Central
PMCID: PMC4079316. http://journals.plos.org/plosone/article?
id=10.1371/journal.pone.0099489.
Goldberg SL, Giardina PJ, Chirnomas D, Esposito J, Paley C, Vichinsky E. The palatability and
tolerability of deferasirox taken with different beverages or foods. Pediatr Blood Cancer
2013;60 9:1507-12. http://www.ncbi.nlm.nih.gov/pubmed/23637051.
Gomez E, Morris CR. Asthma Management in Sickle Cell Disease. Biomed Res Int
2013;2013:604140. http://www.ncbi.nlm.nih.gov/pubmed/24324967.
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Green NS, Ender KL, Pashankar F, Driscoll C, Giardina PJ, Mullen CA, Clark LN, Manwani D,
Crotty J, Kisselev S, Neville KA, Hoppe C, Barral S. Candidate sequence variants and fetal
hemoglobin in children with sickle cell disease treated with hydroxyurea. PLoS One 2013;8
2:e55709. http://www.ncbi.nlm.nih.gov/pubmed/23409025.
Green ST, Martin MB, Haines D, Carson S, Coates T, Oliveros O, Gerstenberger E, Trachtenberg
F, Kwiatkowski JL, Thalassaemia Clinical Research N. Variance of pain prevalence and
associated severity during the transfusion cycle of adult thalassaemia patients. Br J
Haematol 2014;166 5:797-800. http://www.ncbi.nlm.nih.gov/pubmed/24805301.
Grigoriev Y, Lange J, Peterson SM, Takashima JR, Ritchey ML, Ko D, Feusner JH, Shamberger
RC, Green DM, Breslow NE. Treatments and outcomes for end-stage renal disease following
Wilms tumor. Pediatr Nephrol 2012;27 8:1325-33.
http://www.ncbi.nlm.nih.gov/pubmed/22430485.
Haines D, Martin M, Carson S, Oliveros O, Green S, Coates T, Eile J, Schilling L, Dinu B,
Mendoza T, Gerstenberger E, Trachtenberg F, Vichinsky E, Thalassemia Clinical Research N.
Pain in thalassaemia: the effects of age on pain frequency and severity. Br J Haematol
2013;160 5:680-7. http://www.ncbi.nlm.nih.gov/pubmed/23278768.
Hastings C, Gaynon PS, Nachman JB, Sather HN, Lu X, Devidas M, Seibel NL. Increased post-
induction intensification improves outcome in children and adolescents with a markedly
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Marsh A, Schiffelers R, Kuypers F, Larkin S, Gildengorin G, van Solinge W, Hoppe C.
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Nouraie M, Barst R, Kato GJ, Gibbs JS, Sachdev V, Machado RF, Hassell KL, Little JA,
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Polgreen LE, Thomas W, Fung E, Viskochil D, Stevenson DA, Steinberger J, Orchard P, Whitley
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Singer ST, Kuypers F, Fineman J, Gildengorin G, Larkin S, Sweeters N, Rosenfeld H, Kurio G,
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Smith S, Witkowski A, Moghul A, Yoshinaga Y, Nefedov M, de Jong P, Feng D, Fong L, Tu Y, Hu
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Soupene E, Kuypers FA. Phosphatidylcholine formation by LPCAT1 is regulated by Ca(2+)
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Soupene E, Rothschild J, Kuypers FA, Dean D. Eukaryotic protein recruitment into the
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Stookey JD, Klein A, Hamer J, Chi C, Higa A, Ng V, Arieff A, Kuypers FA, Larkin S, Perrier E, Lang
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Suh J, Kanathezhath B, Shenvi S, Guo H, Zhou A, Tiwana A, Kuypers F, Ames B, Walters M.
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Switzer WM, Shankar A, Trimble SR, Thompson AA, Giardina PJ, Cohen AR, Coates TD, Vichinsky
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Tang H, Ho H, Wu P, Chen S, Kuypers FA, Cheng M, Chiu DT. Inability to Maintain GSH Pool in
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Trachtenberg FL, Mednick L, Kwiatkowski JL, Neufeld EJ, Haines D, Pakbaz Z, Thompson AA,
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Treadwell MJ, Anie KA, Grant AM, Ofori-Acquah SF, Ohene-Frempong K. Using Formative
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Treadwell MJ, Bell M, Leibovich SA, Barreda F, Marsh A, Gildengorin G, Morris CR. A Quality
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Trimble S, Reyes N, Thompson A, Giardina P, Cohen A, Coates T, Vichinsky E, Neufeld E,
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Thalassemia Patients in the United States, 2004-2009. 2014 (in process).
Trobaugh-Lotrario AD, Chaiyachati BH, Meyers RL, Haberle B, Tomlinson GE, Katzenstein HM,
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Trobaugh-Lotrario AD, Feusner JH. Relapsed hepatoblastoma. Pediatric Blood & Cancer
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Trobaugh-Lotrario AD, Venkatramani R, Feusner JH. Hepatoblastoma in Children With
Beckwith-Wiedemann Syndrome: Does it Warrant Different Treatment? J Pediatr Hematol
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Tubman VN, Fung EB, Vogiatzi M, Thompson AA, Rogers ZR, Neufeld EJ, Kwiatkowski JL.
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thalassemia longitudinal cohort. J Pediatr Hematol Oncol 2015 (in press).
Ubogy S, Olson K. The Trauma Symptom Checklist for Children and Misdiagnosis of PTSD in
A Youth with Acute Lymphocytic Leukemia: A Brief Report. Journal of Child & Adolescent
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Vichinsky E. Advances in the treatment of alpha-thalassemia. Blood Rev 2012;26 Suppl
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Vichinsky E. Prevalence of medical complications in patients with symptomatic thalassemia
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Vichinsky E. Management of non-transfusion dependent thalassemia (NTDT) & thalassemia
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Vichinsky E, Neumayr L, Neuropsych_Study. The Safety and Efficacy of Transfusion
Compared with Standard Care for the Treatment of Neurologic Dysfunction in Adults with
Sickle Cell Disease. 2014 (in process).
Vichinsky E, Neumayr L, Trimble S, Giardina PJ, Cohen AR, Coates T, Boudreaux J, Neufeld EJ,
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thalassemia patients: a report from the Centers for Disease Control and Prevention
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Vichinsky E, Torres M, Minniti CP, Barrette S, Habr D, Zhang Y, Files B, study CAi. Efficacy and
safety of deferasirox compared with deferoxamine in sickle cell disease: Two-year results
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Vichinsky E. The prevention and management of alloimmunization in sickle cell disease: the
benefit of extended phenotypic matching of red blood cells. Immunohematology 2012;28
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Vichinsky E. Clinical Manifestations of a-Thalassemia. Cold Spring Harb Perspect Med 2013;(3)
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Wagner JE, Jr., Eapen M, Carter S, Wang Y, Schultz KR, Wall DA, Bunin N, Delaney C, Haut P,
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Wahl SK, Garcia A, Hagar W, Gildengorin G, Quirolo K, Vichinsky E. Lower alloimmunization
rates in pediatric sickle cell patients on chronic erythrocytapheresis compared to chronic
simple transfusions. Transfusion 2012;52 12:2671-6.
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Wahl SK, Gildengorin G, Feusner J. Weekend delay in initiation of chemotherapy for acute
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Walter PB, Porter J, Evans P, Kwiatkowski JL, Neufeld EJ, Coates T, Giardina PJ, Grady RW,
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Wun T, Styles L, DeCastro L, Telen MJ, Kuypers F, Cheung A, Kramer W, Flanner H, Rhee S,
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sickle cell anemia. PLoS One 2014;9 7:e101301.
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Yamashita R, Sobota A, Trachtenberg F, Xu Y, Pakbaz Z, Odame I, Thompson A, Haines D,
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Zaky W, Dhall G, Ji L, Haley K, Allen J, Atlas M, Bertolone S, Cornelius A, Gardner S, Patel R,
Pradhan K, Shen V, Thompson S, Torkildson J, Sposto R, Finlay JL. Intensive induction
chemotherapy followed by myeloablative chemotherapy with autologous hematopoietic
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Zhang L, Samad A, Pombo-de-Oliveria MS, Seelo G, Smith MT, Feusner J, Wiemels JL, Buffler
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Fung EB. Bone health in children with special health care needs. J Pediatr Rehabil Med 2014;7
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Klings ES, Morris CR. Making it personal: using genomics to predict pulmonary hypertension
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Vichinsky E. Interventions needed to reduce global burden of sickle cell anemia. HemOnc
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oncology/hematology/news/online/%7B2e438ef2-647e-4aaa-9c7c-d92b3138b88a
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Vichinsky E. Emerging therapy in hemoglobinopathies: lessons from the past and optimism
for the future. Hematol Oncol Clin North Am 2014;28 2:xiii-xviii.
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Letters:
Klings ES, Machado RF, Morris CR, Gordeuk VR, Kato GJ, Ataga KI, Castro O, Hsu L, Telen MJ,
Krishnamurti L, Steinberg MH, Gladwin MT, Diagnosis ATSCGft, Treatment of Pulmonary
Hypertension in Sickle Cell Disease C. Reply: Practice guideline for pulmonary hypertension
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Klings ES, Vichinsky E, Morris CR. Response to "Efficacy and safety of sildenafil for the
treatment of severe pulmonary hypertension in patients with hemoglobinopathies: results
from a long-term follow up " Haematologica 2014;99(2):e17-18. Haematologica 2014;99
2:e19. http://www.ncbi.nlm.nih.gov/pubmed/24497564.
Klings ES, Morris CR, Hsu LL, Castro O, Gladwin MT, Mubarak KK. Pulmonary hypertension of
sickle cell disease beyond classification constraints. J Am Coll Cardiol 2014;63 25 Pt A:2881-
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Reddy-Holdcraft S, Mehta PS, Agrawal AK. Paclitaxel for relapsed or recurrent HIV-
associated pediatric Kaposi's sarcoma. AIDS 2014;28 5:800-2.
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Slone JS, Agrawal AK, Mehta PS, Mazhani L, Motumise K, Anabwani G, Poplack DG. Reply to
"Childhood Cancer in Africa". Pediatr Blood Cancer 2014;61 8:1524.
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Vichinsky E. Safety of deferasirox in sickle cell disease patients with co-existing liver
impairment -- response to Sinakos et.�al. British Journal of Haematology 2012;157 4:506-7.
http://onlinelibrary.wiley.com/doi/10.1111/j.1365-2141.2012.090 38.x/full.
Abstracts:
Abikoff CM, Talano J-A, Keever-Taylor CA, Walters MC, Shenoy S, Moore T, Parsons SK, Dozor
AJ, Friedman D, Chitti R, Shi Q, Grossman BJ, Weinberg RS, Morris E, Brand P, Foley S, Militano
O, Ayello J, Semidei-Pomales M, Baxter-Lowe LA, Cairo MS. Familial Haploidentical (FHI) T-
Cell Depleted (TCD) with T-Cell Addback Stem Cell Transplantation for Patients with
High-Risk Sickle Cell Disease (SCD) (IND 14359). 56th ASH Annual Meeting and
Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2582.
http://www.bloodjournal.org/content/124/21/2582.
Adams-Graves P, Heeney M, Mueller B, Baltz B, Yang E, Paley C, Esposito J, McNamara K,
Vichinsky E. Treatment patterns and clinical outcomes among patients with sickle cell
disease: 24-month follow-up on a 3-year, prospective, non-interventional registry. ASPHO
27th Annual Meeting. Chicago, IL; May 14-17, 2014. Pediatric Blood & Cancer.
http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
Adisa F, Buchanan I, Morris CR. BiPap use in children with sickle cell disease (SCD) and
acute chest syndrome (ACS). 8th Annual Sickle Cell Disease Research and Education
Symposium. Miami, FL; April 2014.
Aguilar A, Kumar A, Saba J. The effect of sphingadiene treatment on neuroblastoma cells.
Sixth CHORI Research Symposium. Oakland, CA: Mar 30, 2012. Children's Hospital & Research
Center Oakland.
Akinsola B, Hagbom R, Zmitrovich A, Kavanagh P, Ashkouti A, Fletcher A, Vinson N, Simon HK,
Fleming A, Jain S, Adisa O, Dampier C, Morris CR. Adding intranasal fentanyl (INF) to the
management of sickle cell disease (SCD) vaso-occlusive pain episodes (VOE) at a
pediatric emergency department (ED): a quality improvement study. 8th Annual Sickle Cell
Disease Research and Education Symposium. Miami, FL; April 2014.
Akinsola B, Hagbom R, Zmitrovich A, Kavanagh P, Ashkouti A, Fletcher A, Vinson N, Simon HK,
Fleming A, Jain S, Adisa O, Dampier C, Morris CR. More rapid delivery of parenteral analgesia
by adding intranasal fentanyl to the management of sickle cell disease vaso-occlusive
pain episodes at a pediatric emergency department. 56th ASH Annual Meeting and
Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).
Allard H, Weyhmiller MG, Lal A, Fung EB. In-Accuracy Of Bone Density Measurements By
DXA In Patients With Hemoglobinopathies and Iron Overload. 54th Annual Meeting of the
American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 966.
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http://bloodjournal.hematologylibrary.org/content/12 2/21/966.abstract.
Alter BP, Giri N, Calvo KR, Maric I, Arthur DC, Hickstein DD, Hastings CA, Lee MA, Hsu A, Holland
SM. Clinically Silent Carriers in Families with Myelodysplastic Syndrome Due to GATA2
Mutations. 54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11,
2012. Blood 120(21); p.1264. http://abstracts.hematologylibrary.org/cgi/
content/abstract/ashmtg;120/21/1264.
Aydinok Y, Galanello R, Viprakasit V, Piga A, Harmatz P, Forni GL, Shah FT, Grace RF, Porter J,
Vichinsky E, Wood J, Krishnan S, Zhang P, Abi-Saab W, Rienhoff HY, Neufeld E. The safety,
tolerability and efficacy of FBS0701, an iron chelator in clinical development for
transfusional iron overload: data from 72 weeks of treatment. 18th Congress of the
European Hematology Association. Stockholm, Sweden: June 13-16, 2013. Haematologica.
Badawy SM, Pinckney K, Meier ER, Myers K, Black V, Hastings CA, Hilden J, Zweidler-McKay PA,
Stork L, Vaiselbuh SR, Johnson TS. First interim analysis of the ASPHO mentoring program.
ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014.
http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
Calloway C, Lee SH, Kim J, Dhillon N, Gildengorin G, Lal A. Mitochondrial Genome Changes As
a Measure Of Iron-Induced Mitochondrial Stress In Transfusion-Dependent Thalassemia.
55th Annual Meeting of the American Society of Hematology. New Orleans, LA; Dec 7-10,
2013. Blood 122(21); 2256. http://bloodjournal.hematologylibrary.org/content/1
22/21/2256.abstract.
Chung J, Feusner J. Utility of hematologic testing for cases of suspected non-accidental
trauma. ASPHO 25th Annual Meeting. New Orleans, LA; May 9-12, 2012. Pediatric Blood &
Cancer 58(7). http://www.connect2conferenc es.com/aspho4/ws_search/index.php?
task=detail&abstract_id=806.
Chung J, Fung EB, Feusner JH. A Pilot Study to Assess Alterations in Trace Element Status
in Pediatric Patients with Malignancies. 54th Annual Meeting of the American Society of
Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.3183.
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Chung J, Lal A, Vichinsky E. Increasing iron overload following splenectomy in Beta
Thalassemia Major. ASPHO Annual Meeting. New Orleans, LA; May 9-12, 2012. Pediatric Blood
& Cancer 58(7); p.1076. http://www.connect2conferenc es.com/aspho4/ws_search/index.php?
task=detail&abstract_id=842.
Delgado EM, Cho CS, Gildengorin G, Leibovich SA, Morris CR. SPeAK Asthma: A study of
pediatric adherence and knowledge of asthma. Pediatric Academy Society Annual Meeting.
Boston, MA; May 2012.
Fens MHAM, Larkin SK, Fitch WL, Scicinski J, Oronsky B, Kuypers FA. Treatment with a Novel
Dinitroazetidine, Abdnaz, Improves Nitrite Reductase Activity of Sickle Red Blood Cells.
54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012.
Blood 120(21); p.3246. http://abstracts.hematologylibrary.org/cgi/
content/abstract/ashmtg;120/21/3246.
Fleming A, Jain S, Adisa O, Dampier C, Morris CR. Intranasal fentanyl use improves time to
first parenteral analgesia in children with sickle cell disease vaso-occlusive pain episodes
at a pediatric emergency department. Pediatric Academy Society Annual Meeting. San Diego,
CA; April 2015.
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Fung E. Low Magnitude Mechanical Stimulation Increases Bone Mass in Adult Patients with
Thalassemia: A Pilot Study. Sixth CHORI Research Symposium. Oakland, CA: Mar 30, 2012.
Children's Hospital & Research Center Oakland.
Fung EB, Killilea DW, Shenvi S, Haines D, Lavrisha L, Flores B, Higa A, Ahmad T, Lal A. Marginal
zinc status associated with altered insulin metabolism in patients with thalassemia. 4th
International Society for Zinc Biology Meeting. Asilomar, CA; Sep 14-19, 2014. poster
presentation, abstract #FF10.
Fung EB, Kwiatkowski JL, Huang JN, Gildengorin G, King JC, Queisser AC, Vichinsky E. Zinc
supplementation improves bone density in young adults with thalassemia. 6th
International Conference on Children's Bone Health; June 2013. Rotterdam, Netherlands.
Fung EB, Reget K, Sawyer A, Haines D, Lal A. Exploring vertebral abnormalities in patients
with thalassemia and sickle cell disease. 6th International Conference on Children's Bone
Health. Rotterdam, Netherlands; June 2013.
Fung EB, Sushrita N, Haines D, Schroepfer C, Lal A. Dietary Intake Insufficient to Support
Nutritional Adequacy in Patients with Thalassemia. 56th ASH Annual Meeting and
Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 1361-.
http://www.bloodjournal.org/content/124/21/1361.
Galanello R, Aydinok Y, Piga A, Forni GL, Viprakasit V, Harmatz P, Shah F, Grace R, Vichinsky E,
Wood J, Peppe J, Jones A, Rienhoff HY, Neufeld E. A 48 week phase 2 study of the safety,
tolerability and efficacy of FBS0701, a novel iron chelator for treatment of transfusional
iron overload. 17th Congress of the European Hematology Association. Amsterdam, The
Netherlands: June 14-17, 2012. Haematologica 97(s1); #0606. http://
www.ehaweb.org/congress-and-events/18th-congress/previous-congresses-2/abstract-
book/eha-17-amsterdam-2012/.
Gladwin MT, Barst RJ, Gibbs JS, Hildesheim M, Sachdev V, Nouraie M, Hassell KL, Little JA,
Schraufnagel DE, Krishnamurti L, Novelli E, Girgis RE, Morris CR, Berman Rosenzweig E,
Badesch DB, Lanzkron S, Castro OL, Taylor JGt, Goldsmith JC, Kato GJ, Gordeuk VR, Machado
RF, Walk Phaast investigators. Risk factors for death in 632 patients with sickle cell
disease in the United States and United Kingdom. 54th Annual Meeting of the American
Society of Hematology. Atlanta, GA; Dec 8-11, 2012.
Gomez E, Calloway C, Hoon Lee S, Kim J, Dhillon N, Gildengoren G, Lal A. Mitochondrial
genome changes as a measure of iron-induced mitochondrial stress in transfusion-
depedent thalassemia. 55th Annual Meeting of the American Society of Hematology. New
Orleans, LA; Dec 7-10, 2013. Blood 122(21); 2256.
http://bloodjournal.hematologylibrary.org/content/1 22/21/2256.abstract.
Hacker NA, King JC, Van Loan MD, Gertz ER, Adams M, Sawyer A, Fung EB. Calcium
supplementation during pregnancy improves tibial bone density at one year post-partum
in racially diverse women. Experimental Biology, April 2014. San Diego, CA. #14-7168.
Haines D. Pain in Thalassemia: Pervasive and Severe. 2nd Meeting of the Worldwide Initiative
on Social Studies on Hemoglobinopathies. Atlanta, GA: March 16, 2012. poster presentation.
Heeney MM, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E,
George A. Comparison of Clinical Outcomes Between Adult and Pediatric Patients (pts)
with Sickle Cell Disease (SCD): 3-Year (y) Follow-up in a Prospective, Longitudinal,
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Noninterventional Registry Trial. 56th ASH Annual Meeting and Exposition. San Francisco,
CA; Dec 6-9, 2014. Blood 124(21); 4890-. http://www.bloodjournal.org/content/124/21/4890.
Heeney MM, Mueller BU, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, Vichinsky E. 12-
Month Follow-up for Patients with Sickle Cell Disease in an Ongoing 3-Year, Prospective,
Non-Interventional Registry Trial. 54th Annual Meeting of the American Society of
Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.1010.
http://abstracts.hematologylibrary.org/cgi/ content/abstract/ashmtg;120/21/1010.
Hoehner C, Hagar RW. A Dedicated Over 50 Sickle Cell Clinic. 6th Annual Sickle Cell Disease
Research and Educational Symposium and Annual National Sickle Cell Scientific Meeting.
Hollywood, Florida; Feb 29-Mar 2, 2012. Am J Hematol 87(7).
http://onlinelibrary.wiley.com/doi/10.1002/ajh.23331/abstrac t.
Jacobs J. Invasive Pulmonary Aspergillosis in Pediatric Oncology Patients. ASPHO 26th
Annual Meeting. Miami, FL; April 24-27, 2013. Pediatric Blood & Cancer 60(S2).
http://www.connect2conferen ces.com/aspho4/ws_search/index.php?
task=detail&abstract_id=1243.
Jubran RF, Leavey PJ, Ritchey AK, Tersak JM, Hastings C, Briones M, Shereck E, Nyquist J,
Fisher D. Career development for pediatric hematology/oncology (PHO) fellows: a pilot
program. ASPHO 26th Annual Meeting. Miami, FL; April 24-27, 2013. Pediatric Blood & Cancer
60(S2). http://www.connect2conferen ces.com/aspho4/ws_search/index.php?
task=detail&abstract_id=1243.
Kamani NR, Walters M, Carter S, Brochstein JA, Eapen M, Levine JE, Logan B, Panepinto J,
Parikh S, Pulsipher M, Schultz KR, Shenoy S. Unrelated Donor Cord Blood Transplantation
For Children With Severe Sickle Cell Disease: Results Of A Phase Ii Study From The Blood
And Marrow Transplant Clinical Trials Network. BMT Tandem Meetings. San Diego, CA: Feb.
1-5, 2012. American Society for Blood and Marrow Transplantation #327.
http://www.abstracts2view.com/bmt/view.php?nu=ASBMT12L_372
Kanathezhath B, Shenvi S, Johl A, Manmohan R, Bhandhal MK, Oh D, Zhou A, Kuypers FA,
Walters MC, Ames BN, Suh J. Systemic And Hepatic Thiol Redox Dysregulation In Graft
Versus Host Disease. BMT Tandem Meetings. San Diego, CA: Feb. 1-5, 2012. American Society
for Blood and Marrow Transplantation #421. http://www.abstracts2view.com/bmt/view.php?
nu=ASBMT12L_259.
Kanathezhath B, Suh J, Shenvi S, Guo H, Walters M, Ames B. Glutathione Redox Metabolomic
Dysregulation Precedes TNF-? Elevation and Predicts Severity of Gvhd in Experimental
Transplantation. BMT Tandem Meetings. Salt Lake City, Utah: Feb. 13-17, 2013. American
Society for Blood and Marrow Transplantation #438.
https://bmt.confex.com/tandem/2013/webprogram/Paper2122.html.
Keller SD, Treadwell MJ, Yang M, Werner EM, Hassell KL. Patient reports of health outcomes
in sickle cell disease: psychometric properties of the Adult Sickle Cell Quality of Life
Measurement System. 2nd Global Congress on Sickle Cell Disease. Rio de Janiero, Brazil:
November 11-14, 2014. http://www.hemorio.rj.gov.br/CongressoGSCDN/programa.pdf.
Khurana M, Feusner JH, Lee B. Fever at diagnosis of pediatric acute lymphoblastic leukemia
(ALL): Are antibiotics really necessary. American Society of Clinical Oncology Annual
Meeting. Chicago, Illinois; June 1-5, 2012. Abstract #9553.
http://meetinglibrary.asco.org/content/101090-114.
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Khurana M, Kanathezhath B, Feusner J. Recurrent/refractory metastatic osteosarcoma
responds to TRAIL therapy. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014.
http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
Khurana M, Vichinsky E, Theil EC. Head-to-head comparison of current clinical iron chelators
on cellular ferritin regulation in HEPG2 cell culture model. ASPHO 27th Annual Meeting.
Chicago, IL; May 14-17, 2014. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.
Klein O, Walters M, George D, Chu R, Goodrich JT, Roman E, Schubert R, Del Toro G.
Moyamoya Syndrome Treated With Encephaloduroarteriosynangiosis Followed By
Hematopoietic Cell Transplantation In Patients With Sickle Cell Disease. BMT Tandem
Meetings. San Diego, CA: Feb. 1-5, 2012. American Society for Blood and Marrow Transplantation
#276. http://www.abstracts2view.com/bmt/view.php?nu=ASBMT12L_344
Kutlar A, Reid M, Taher AT, Inati A, Abboud MR, El-Beshlawy A, Buchanan GR, Smith H, Ataga
KI, Koshy N, Neumayr LD, Malik P, Alvarez OA, Ward R, White JM, Johnson E, Ghalie RG. A
Randomized, Open-Label, Multicenter, Dose Escalation Study of HQK-1001 (2,2-
Dimethylbutyrate, Sodium Salt) in Sickle Cell Disease. 54th Annual Meeting of the American
Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.998.
http://abstracts.hematologylibrary.org/cgi/c ontent/abstract/ashmtg;120/21/998.
Kutny MA, Alonzo TA, Gerbing RB, Wang Y-C, Fu C, Meshinchi S, Gamis AS, Feusner JH, Gregory
J. Arsenic Trioxide Is a Well Tolerated Consolidation Regimen in Children with Newly
Diagnosed Acute Promyelocytic Leukemia; Toxicity Results of the Children�s Oncology
Group AAML0631 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9,
2014. Blood 124(21); 985-. http://www.bloodjournal.org/content/124/21/985.
Kutny MA, Geyer S, Laumann KM, Gregory J, Willman CL, Stock W, Larson RA, Powell BL,
Feusner JH. A Comparison of Outcomes Between Adolescents and Young Adults (AYA) and
Children with Acute Promyelocytic Leukemia (APL): North American Intergroup Study
CALGB 9710 (Alliance). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-
9, 2014. Blood 124(21); 2306-. http://www.bloodjournal.org/content/124/21/2306.
Kutny MA, Geyer S, Laumann KM, Gregory J, Willman CL, Stock W, Larson RA, Powell BL,
Feusner JH. Effect of Young Age on Outcomes in Pediatric Acute Promyelocytic Leukemia
(APL): North American Intergroup Study CALGB 9710 (Alliance). 56th ASH Annual Meeting
and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2301-.
http://www.bloodjournal.org/content/124/21/2301.
Kutny MA, Rajpurkar M, Alonzo TA, Gerbing RB, Gamis AS, Feusner JH, Gregory J. Evaluation of
ISTH DIC Score to Predict Significant Bleeding and Thrombosis Events in Pediatric Acute
Promyelocytic Leukemia; A Report from the Children�s Oncology Group AAML0631 Trial.
56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21);
3669-. http://www.bloodjournal.org/content/124/21/3669.
Lal A, Patterson L, Goldrich A, Marsh A, Yen K, Bhatnagar A. Detection of elevated end-tidal
carbon monoxide concentration in children with sickle cell anemia. PAS/ASPR Joint Meeting.
Vancouver, Canada: May 3-6, 2014. Pediatric Academic Societies and Asian Society for Pediatric
Research.
Lal A, Yen K, Patterson L, Goldrich A, Marsh AM, Bhatnagar A. Elevated End-Tidal Carbon
Monoxide Concentration in Children with Sickle Cell Anemia. 56th ASH Annual Meeting and
Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 1390-.
2/18/15 Hematology/Oncology Department: Recent Faculty Publications (2012-2015), UCSF Benioff Children's Hospital Oakland
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http://www.bloodjournal.org/content/124/21/1390.
Lalefar N, Agarwal R, Porteus M, Kharbanda S, Weinberg K. Bortezomib As a Treatment for
Autoimmune Cytopenia After Bone Marrow Transplant. BMT Tandem Meetings. Salt Lake
City, Utah: Feb. 13-17, 2013. American Society for Blood and Marrow Transplantation #125.
Lalefar N, Ozeran J. Iron Overload in Childhood Cancer. ASPHO 25th Annual Meeting. New
Orleans, LA; May 9-12, 2012. Pediatric Blood & Cancer 58(7). http://www.connect2conferenc
es.com/aspho4/ws_search/index.php?task=detail&abstract_id=687.
Lalefar NR, Walters M. Graft failure after hematopoietic cell transplantation for
hemoglobionpathies; successful rescue with alternate donors. Annual Sickle Cell Disease
Research and Educational Symposium and 37th National Sickle Cell Disease Scientific Meeting.
Miami, FL; April 11-14, 2014.
Latronica C, Kuypers FA, Rosenfeld H, Larkin SK, Doniger S, Vichinsky E, Morris CR. Tricuspid
Regurgitant Jet Velocity (TRV), Biomarkers of Hemolysis, and Impact of Oxygen Therapy
in Children with Sickle Cell Disease (SCD) and Vaso-Occlusive Pain Episodes (VOE). 54th
Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood
120(21); p.4752. http://abstracts.hematologylibrary.org/cgi/
content/abstract/ashmtg;120/21/4752.
Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris CR. Are we missing the mark?
Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest
syndrome (ACS). Pediatric Academy Society Annual Meeting. San Diego, CA; April 2015.
Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris CR. Are we missing the mark?
Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest
syndrome (ACS). 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL;
April 2014.
Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris CR. Are we missing the mark?
Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest
syndrome (ACS). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014.
Blood 124(21).
Lee JH, Rademaker AW, Powell BL, Geyer S, Larson RA, Gregory J, Hijiya N, Feusner JH.
Obesity Does Not Affect the Recurrence Free Survival Rates in Children Less Than 20
Years of Age in Acute Promyelocytic Leukemia (APL). 56th ASH Annual Meeting and
Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 957-.
http://www.bloodjournal.org/content/124/21/957.
Lew G, Lu X, Yanofsky R, Rheingold SR, Whitlock J, An Q, Devidas M, Hastings CA, Winick NJ,
Carroll WL, Borowitz MJ, Hunger S, Pulsipher MA. Outcomes after Intermediate-Risk Relapse
of Childhood B-Lymphoblastic Leukemia (B-ALL) and the Role of Allogeneic Stem Cell
Transplantation (SCT): A Report from Children's Oncology Group (COG) AALL0433. 56th
ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 684-.
http://www.bloodjournal.org/content/124/21/684.
Lew G, Lu X, Yanofsky RA, Rheingold SR, Whitlock JA, Gulig SD, Devidas M, Pulsipher MA,
Hastings CA, Winick NJ, Carroll WL, Borowitz MJ, Hunger SP. The significance of minimal
residual disease (MRD) in relapsed childhood B-lymphoblastic leukemia: Interim analysis
of Children's Oncology Group (COG) protocol AALL0433. ASCO Annual Meeting. Chicago,
IL; May 30-June 3, 2014. J Clin Oncol 32:5s(2014 suppl ); abstr 10014.
2/18/15 Hematology/Oncology Department: Recent Faculty Publications (2012-2015), UCSF Benioff Children's Hospital Oakland
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Magnani JL, Kuypers FA, Patton JT, Larkin SK, Styles L, DeCastro LM, Telen MJ, Wun T,
Thackray H. Pan-Selectin Antagonist GMI-1070 Affects Biomarkers of Adhesion, Activation
and the Coagulation Cascade in Sickle Cell Adults At Steady State. 54th Annual Meeting of
the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.87.
http://abstracts.hematologylibrary.org/cgi/co ntent/abstract/ashmtg;120/21/87.
Majerus EM, Ataga KI, Vichinsky E, Eaton CA, Mazanet R, Nathan DG, Field JJ. NKTT120
Reduces iNKT Cells without Dose Limiting Toxicity in Stable Adult Sickle Cell Patients in a
Phase 1 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014.
Blood 124(21); 2718-. http://www.bloodjournal.org/content/124/21/2718.
Marsh A, Feusner J, Cham E. Are bone marrow core biopsies necessary for the initial
diagnosis of acute leukemia? ASPHO 25th Annual Meeting. New Orleans, LA; May 9-12, 2012.
Pediatric Blood & Cancer 58(7). http://www.connect2conferenc
es.com/aspho4/ws_search/index.php?task=detail&abstract_id=783.
Marsh AM, Quirolo KC, Golden C, Vichinsky E. Renal Medullary Carcinoma in an Adolescent
with Homozygous Hemoglobin SS. 54th Annual Meeting of the American Society of
Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.4774.
http://abstracts.hematologylibrary.org/cgi/ content/abstract/ashmtg;120/21/4774.
Minor M, Harmatz P, Fuentebella J, Haines D, Lal A, Vichinsky E. Practical management of HCV
genotype 1a in B thalassemia major with triple therapy. Viral Hepatitis Congress 2012.
Frankfurt, Germany; Sep 7-9 2012. . Journal of Viral Hepatitis 19(s3); 10. <Go to
ISI>://WOS:000308584500020
Morris CR, Kuypers FA, Lavrisha L, Sweeters N, Stewart M, Ansari M, Neumayr L, Vichinsky EP.
Arginine therapy: a novel treatment for children with sickle cell disease and vaso-
occlusive pain. First Conference of the International Rare Diseases Research Consortium
(IRDiRC). Dublin, Ireland; April 2013.
Morris C, Latronica C, Kuypers FA, Rosenfeld H, Larkin SK, Doniger S, Vichinsky E, Shiva S.
Citrate Synthase Activity Is Increased In Children With Sickle Cell Disease (SCD) On
Hydroxyurea (HU) Therapy. 8th Annual Sickle Cell Disease Research and Education
Symposium. Miami, FL; April 2014.
Morris C, Latronica C, Kuypers FA, Rosenfeld H, Larkin SK, Doniger S, Vichinsky E, Shiva S.
Citrate Synthase Activity Is Increased In Children With Sickle Cell Disease (SCD) On
Hydroxyurea (HU) Therapy. 55th Annual Meeting of the American Society of Hematology.
New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 4690.
http://bloodjournal.hematologylibrary.org/content/1 22/21/4690.abstract.
Morris CR, Barreda F, Leibovich SA, Rutherford M, Saulys A, Stewart M, Lavrisha L, Vichinsky E,
Bell M, Treadwell MJ. Quality Improvement Goals for Sickle Cell Disease Pain Management
in an Urban Pediatric Emergency Department: We Can Do Better! 54th Annual Meeting of
the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.2101.
http://abstracts.hematologylibrary.org/cgi/ content/abstract/ashmtg;120/21/2101.
Morris CR, Barreda F, Leibovich SA, Rutherford M, Saulys A, Stewart M, Lavrisha L, Vichinsky E,
Bell M, Treadwell MJ. Quality improvement initiatives for sickle cell disease pain
management in an urban pediatric emergency department significantly improves
outcomes. Pediatric Academic Societies Annual Meeting; May 4-7, 2013. Washington, DC.
http://www.abstracts2view.com/pas/view.php?nu=PAS13L1_4523. 443.
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Morris CR, Kim H-Y, Wood JC, Trachtenberg F, Klings ES, Porter JB, Sweeters N, Olivieri NF,
Kwiatkowski JL, Singer ST, Taher AT, Neufeld EJ, Thompson AA, Larkin SK, Suh JH, Vichinsky E,
Kuypers FA. Cardiopulmonary and Laboratory Profiling of Patients with Thalassemia At
Risk for Pulmonary Hypertension: Report From the Thalassemia Clinical Research
Network. 54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11,
2012. Blood 120(21); p.2122. http://abstracts.hematologylibrary.org/cgi/
content/abstract/ashmtg;120/21/2122.
Morris CR, Kim H-Y, Wood JC, Trachtenberg F, Klings ES, Porter JB, Sweeters N, Olivieri NF,
Kwiatkowski JL, Singer ST, Taher AT, Neufeld EJ, Thompson AA, Sachdev V, Larkin SK, Suh JH,
Kuypers FA, Vichinsky E. Sildenafil Therapy in Patients with Thalassemia and an Elevated
Tricuspid Regurgitant Jet Velocity (TRV) On Doppler Echocardiography At Risk for
Pulmonary Hypertension: Report From the Thalassemia Clinical Research Network. 54th
Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood
120(21); p.1023. http://abstracts.hematologylibrary.org/cgi/
content/abstract/ashmtg;120/21/1023.
Morris CR, Kuypers FA, Lavrisha L, Sweeters N, Stewart M, Ansari M, Neumayr L, Vichinsky EP.
Randomized, placebo-controlled trial of arginine therapy for the treatment of children with
sickle cell disease and vaso-occlusive pain episodes. NHLBI workshop: Translating new
therapeutics for sickle cell disease to the marketplace; August 21, 2013; National Institutes of
Health, Bethesda MD.
Morris HD, Feusner JH, Wilson KS, Aquino V, Levenson B, Timmons M, Cavalier M, Luu H.
Therapy-induced t(11;19)(q23;q13.1) with relapsed acute promyelocytic leukemia.
ASPHO 26th Annual Meeting. Miami, FL; April 24-27, 2013. Pediatric Blood & Cancer 60(S2); 895.
http://www.connect2conferenc es.com/aspho4/ws_search/index.php?
task=detail&abstract_id=895.
Morris HD, Feusner JH, Wilson KS, et.al. Therapy-induced t(11;19)(q23;q13.1) with
relapsed acute promyelocytic leukemia. Association of Molecular Pathology Annual Meeting.
May 2012.
Mueller BU, Baltz B, Adams-Graves P, Yang E, Paley C, MSHS JE, MSHS CCRA MK, Vichinsky E.
Clinical Outcomes For Patients With Sickle Cell Disease: 24-Month Follow-Up In An
Ongoing 3-Year, Prospective, Non-Interventional Registry Trial. 55th Annual Meeting of
the American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 988.
http://bloodjournal.hematologylibrary.org/content/12 2/21/988.abstract.
Murray L, Walters MC, Chaudhury S, Soni S, Pulsipher MA, Schultz KR, Chan K, Nieder M,
Loechelt B, Parikh SH, Kasow KA, Haight A, Hale GA, Connelly J, Andreansky M, Trachtenberg F,
Neufeld EJ, Kwiatkowski J, DiFronzo NL, Thompson AA. Multicenter Investigation Of
Unrelated Donor Hematopoietic Cell Transplantation (HCT) For Thalassemia Major After a
Reduced Intensity Conditioning Regimen (URTH Trial). 55th Annual Meeting of the American
Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 543.
http://bloodjournal.hematologylibrary.org/content/12 2/21/543.abstract.
Novelli EM, Delaney K, Axelrod K, Morris CR, Minniti C. Arginine therapy in a patient with Hb-
SS disease and refractory leg ulcers. Sickle Cell Disease Association of America Annual
Convention. Baltimore, MD; Sept 2012.
Paulukonis S, Currier R, Coates TD, Vichinsky E, Feuchtbaum L. Impact of Immigration and
Migration on Thalassemia Surveillance in California, 2004-2008. 56th ASH Annual Meeting
2/18/15 Hematology/Oncology Department: Recent Faculty Publications (2012-2015), UCSF Benioff Children's Hospital Oakland
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and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4855-.
http://www.bloodjournal.org/content/124/21/4855.
Paulukonis S, Griffin T, Zhou M, Eckman JR, Hagar R, Bauer Snyder A, Feuchtbaum L, Grant AM,
Hulihan M. Sickle Cell Disease Mortality in California and Georgia 2004-2008. 56th ASH
Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 439-.
http://www.bloodjournal.org/content/124/21/439.
Porter J, Walter PB, Neumayr LD, Evans P, Weyhmiller MG, Harmatz P, Wood JC, Miller JL,
Weiss G, Yuan Q, Wang ZJ, Grosse R, Schoennagel BP, Meerpohl J, Fischer R, Nielsen P, Seifert
M, Vichinsky E. Inflammatory and Vitamin Bio-Markers Of Iron Trafficking and Distribution
In Transfusional Overload: Insights From Comparing Diamond Blackfan Anemia With
Sickle Cell Disease and Thalassemia (MCSIO PILOT Study). 55th Annual Meeting of the
American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 1014.
http://bloodjournal.hematologylibrary.org/content/1 22/21/1014.abstract.
Porter JB, Walter PB, Neumayr LD, Evans P, Weyhmiller MG, Harmatz P, Wood JC, Miller JL,
Weiss G, Yuan Q, Wang ZJ, Grosse R, Schoennagel BP, Meerpohl J, Fischer R, Seifert M,
Vichinsky E. Bio-markers of Iron Trafficking and Distribution in Transfusional Overload:
Insights from Comparing Diamond Blackfan Anemia with Sickle Cell Disease and
Thalassemia (MCSIO Pilot Study). International BioIron Society Meeting. University College
London; April 14-18, 2013.
Porter JB, Walter PB, Neumayr LD, Evans P, Weyhmiller MG, Harmatz P, Wood JC, Miller JL,
Weiss G, Yuan Q, Wang ZJ, Grosse R, Schoennagel BP, Meerpohl J, Fischer R, Vichinsky E. Iron
Trafficking and Distribution in Transfusional Overload: Insights From Comparing Diamond
Blackfan Anemia with Sickle Cell Disease and Thalassemia. 54th Annual Meeting of the
American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.995.
http://abstracts.hematologylibrary.org/cgi/c ontent/abstract/ashmtg;120/21/995.
Radhakrishnan K, Talano J, Keever-Taylor C, Bhatia M, Shenoy S, Walters M, Parsons S, Morris
E, Baxter-Lowe LA, Cairo MS. Familial Haploidentical (FHI) T-Cell Depleted (TCD)
Transplantation In High-Risk Sickle Cell Disease (IND 14359). BMT Tandem Meetings. San
Diego, CA: Feb. 1-5, 2012. American Society for Blood and Marrow Transplantation #265.
http://www.abstracts2view.com/bmt/view.php?nu=ASBMT12L_203
Schiffelers R, Gildengorin G, Kuypers FA, Hoppe C. Microparticles As Biomarkers Of
Osteonecrosis Of The Hip In Sickle Cell Disease. 55th Annual Meeting of the American
Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 2226.
http://bloodjournal.hematologylibrary.org/content/1 22/21/2226.abstract.
Singer ST, Wang J, Suh JH, Killelea D, Ivani K, Oliveros O, Yuan Q, Vichinsky E, Smith J.
Abnormal Reproductive Measures and Seminal Plasma Findings in Men With Thalassemia
Major (TM) and Iron Overload. 55th Annual Meeting of the American Society of Hematology.
New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 4707.
http://www.bloodjournal.org/content/122/21/4707.
Singer ST, Wang J, Yuan Q, Vichinsky E, Smith J, Paley C, Fischer R. Pituitary Iron and Volume
Are Affecting Hormones and Reproductive Potential. 56th ASH Annual Meeting and
Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4048.
https://ash.confex.com/ash/2014/webprogram/Paper75574.html.
Suh JH, Kanathezhath B, Swapna S, Guo H, Walters MC, Ames BN. Host Nrf2 -glutathione
2/18/15 Hematology/Oncology Department: Recent Faculty Publications (2012-2015), UCSF Benioff Children's Hospital Oakland
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Redox Dysregulation Precedes TNF-{alpha} Elevation and Predicts Severity of Graft
Versus Host Disease in Experimental Transplantation. 54th Annual Meeting of the American
Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.4107.
http://abstracts.hematologylibrary.org/cgi/ content/abstract/ashmtg;120/21/4107.
Thompson AA, Rasko JE, Hongeng S, Kwiatkowski JL, Schiller G, von Kalle C, Cavazzana M,
Leboulch P, Petrusich A, Soni S, Walters MC. Initial Results from the Northstar Study (HGB-
204): A Phase 1/2 Study of Gene Therapy for ?-Thalassemia Major Via Transplantation of
Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral ??-T87Q -
Globin Vector (LentiGlobin BB305 Drug Product). 56th ASH Annual Meeting and Exposition.
San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 549. Nominated for Best of ASH abstract.
http://www.bloodjournal.org/content/124/21/549.
Treadwell M, Paulukonis S, Currier B, Hutchinson C, Neumayr L, Vichinsky E, Feuchtbaum L.
Population-based study of mental health diagnoses and utilization in sickle cell disease.
Annual Sickle Cell Disease Research and Educational Symposium and 37th National Sickle Cell
Disease Scientific Meeting. Miami, FL; April 11-14, 2014. poster presentation.
Treadwell M, Johnson S, Sisler I, Gildengorin G, Medina R, Barreda F, Bitsko M, Smith WR.
Evaluation of a sickle cell disease specific readiness for transition assessment. 8th Annual
Sickle Cell Disease Research & Educational Symposium and 37th National Sickle Cell Disease
Scientific Meeting. Miami, FL. April 11-14, 2014. Journal of Sickle Cell Disease and
Hemoglobinopathies 2014(1; doi 10.14223/JSCDH-D-14-00081).
Treadwell MJ, Anie K, Asafo M, Creary M, Dennis-Atwi J, grant A, Lamptey M, Ojodu J, Otaigbe
A, Yusuf C, Ohene-Frempong K. Development Workshop for a Sickle Cell Counselor Training
and Certification Program in Ghana. SCDAA 41st Annual Convention; Sept 25-27, 2013.
Baltimore, MD.
Treadwell MJ, Barreda F, Payton W, Sydnor V, Murphy W. Using Multidimensional Strategies
to Improve Adherence with Iron Chelation Therapies. SCDAA 41st Annual Convention; Sept
25-27, 2013. Baltimore, MD.
Treadwell MJ, Bell M, Leibovich SA, Barreda F, Marsh A. Quality improvement initiative
improves emergency department care for pediatric patients with sickle cell disease. UCSF
Seventh Annual Health Disparities Research Symposium. Oct 23, 2013; San Francisco, CA.
Trobaugh-Lotrario AD, Chaiyachati BH, Meyers R, Haberle B, Tomlinson GE, Katzenstein HM,
Malogolowkin MH, von Schweinitz D, Krailo MD, Feusner JH. Outcome in congenital
hepatoblastoma compared with previously reported data. 2013 ASCO Annual Meeting. May
30 - Jun 3, 2014; Chicago, Illinois. American Society of Clinical Oncology.
http://meetinglibrary.asco.org/content/118312-132.
Vichinsky E. Fetal hemoglobin and its relationship to CNS disease in hemoglobinopathies.
18th Annual Hemoglobin Switching Conference. Monterey, California; June 7-11, 2012.
Vichinsky E, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, George A,
Heeney MM. Clinical complications in pediatric and adult sickle cell disease. Association of
Pediatric Hematology/Oncology Nurses (APHON) Annual Conference & Exhibit. Portland, OR; Sep
4-6 2014. poster presentation.
Vichinsky E, Beshlawy AE, Alzoebie A, Bernaudin F, Koussa S, Chotsampancharoen T, El-Ali A,
Arrowsmith C, Martin M, El-Alfy M. Long-term safety and effectiveness of deferasirox
(Exjade�) in pediatric patients aged 2�<6 years at enrollment: Interim report from a 5-
2/18/15 Hematology/Oncology Department: Recent Faculty Publications (2012-2015), UCSF Benioff Children's Hospital Oakland
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year observational study. 3rd Pan-European Conference on Haemoglobinopathies and Rare
Anaemias. Limassol, Cyprus: Oct 24-26, 2012.
Vichinsky E, El-Beshlawy A, Alzoebie A, Bernaudin F, Koussa S, Chotsampancharoen T, El-Ali A,
Arrowsmith C, Martin N, El-Alfy M. Interim Safety and Effectiveness Results From a 5-Year
Observational Study of Deferasirox in Pediatric Patients Aged 2-<6 Years At Enrollment.
54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012.
Blood 120(21); p.2125. http://abstracts.hematologylibrary.org/cgi/
content/abstract/ashmtg;120/21/2125.
Vichinsky E. Neuropsychological Dysfunction And Neuroimaging Abnormalities In
Neurologically Intact Adults with SCD. 6th Annual Sickle Cell Disease Research and
Educational Symposium and Annual National Sickle Cell Scientific Meeting. Hollywood, Florida;
Feb 29-Mar 2, 2012. oral presentation.
Vichinsky E. Clinical Aspects of Iron Overload: Causes, Diagnosis, Complications,
Treatment, Outcomes. Society for Pediatric Radiology 55th Annual Meeting & Postgraduate
Course. San Francisco, California; April 19, 2012. Pediatr Radiol 42, Issue 2 Supplement(2);
oral presentation. http://link.springer.com.ucsf.idm.oclc.org/article/10.1007/s00247-012-2356-
8/fulltext.html.
Walter PB, Harmatz P, Higa A, Ng V, Weyhmiller MG, Evans P, Porter JB, Sweeters N, Price J,
Manji A, Killilea D, Lal A, Vichinsky E. Innate Immune Cell Expression of Pattern Recognition
Receptors From {beta}-Thalassemia Patients During Intensive Combination Chelation
Therapy. 54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11,
2012. Blood 120(21); p.1025. http://abstracts.hematologylibrary.org/cgi/
content/abstract/ashmtg;120/21/1025.
Walter PB, Harmatz P, Higa A, Ng V, Weyhmiller MG, Evans P, Porter JB, Sweeters N, Price J,
Manji A, Killilea D, Lal A, Vichinsky E. Innate Immune Cell Expression of Pattern Recognition
Receptors from Transfused Thalassemia Major Patients During Intensive Combination
Chelation Therapy. International BioIron Society Meeting. University College London; April 14-
18, 2013.
Walter PB, Higa A, Ng V, Weyhmiller MG, Slater NR, Evans P, Porter JB, Sweeters N, Price J,
Manji A, Killilea D, Lal A, Vichinsky E. Association Of Cardiac Iron By T2* With Innate
Immune Markers In Transfusion-Dependent Thalassemia Patients Undergoing Combined
Chelation Therapy. 55th Annual Meeting of the American Society of Hematology. New
Orleans, LA; Dec 7-10, 2013. Blood 122(21); 3450.
http://bloodjournal.hematologylibrary.org/content/1 22/21/3450.abstract.
Walter PB, Pakbaz Z, Nemeth E, Ganz T, Porter JB, Evans P, Houston KM, Fischer R, Weyhmiller
MG, Herz M, Miller JL, Hagar R, Neumayr LD, Vichinsky E, Harmatz P. Determinants Of Tissue
Iron Loading In Transfused and Non-Transfused ?-Thalassemia and Sickle Cell Disease
Patients � Biomarkers Of Iron Regulation and Inflammation. 55th Annual Meeting of the
American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 1017.
http://bloodjournal.hematologylibrary.org/content/1 22/21/1017.abstract.
Walter PB, Hohman L, Rokeby A, Manocha A, Lum JJ, Lavrisha L, Stewart M, Hagar R, Vichinsky
E, Morris CR. The effects of glutamine supplementation on markers of autophagy and
apoptosis in peripheral blood mononuclear cells from patients with sickle cell disease. Free
Radical Biology and Medicine. Seattle, WA; Nov 2014.
2/18/15 Hematology/Oncology Department: Recent Faculty Publications (2012-2015), UCSF Benioff Children's Hospital Oakland
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Walter PB, Hohman L, Rokeby A, Manocha A, Lum JJ, Lavrisha L, Stewart M, Hagar R, Vichinsky
E, Morris CR. The effects of glutamine supplementation on markers of autophagy and
apoptosis in peripheral blood mononuclear cells from patients with sickle cell disease.
56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).
Walters MC, Sandmaier BM, Storb R, D. Flowers ME, Deeg HJ, O'Donnell P, Woolfrey AE, Kiem
H-P. Modulated Cyclophosphamide-Based In Vivo T-Cell Depletion Promotes Engraftment
With Minimal Gvhd and Low Toxicity In Fanconi Anemia Patients. 55th Annual Meeting of
the American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 4561.
http://bloodjournal.hematologylibrary.org/content/1 22/21/4561.abstract.
Wang J, Suh JH, Killelea D, Ivani K, Oliveros O, Yuan Q, Vichinsky E, Smith J. Abnormal
Reproductive Measures and Seminal Plasma Findings in Men With Thalassemia Major
(TM) and Iron Overload. 55th Annual Meeting of the American Society of Hematology. New
Orleans, LA; Dec 7-10, 2013. Blood 122(21); 4707.
http://bloodjournal.hematologylibrary.org/content/1 22/21/4707.abstract.
Wang Z, Diaw L, Dizon M, Barr M, Quinn M, Diggs D, Allen D, Seamon C, Oguhebe A, Darbari D,
Zhang Y, Gladwin MT, Hutchinson AA, Burdette L, Hoppe C. Admixture In Sickle Cell Disease
Defined By Genome Wide Ancestry Informative Markers Varies By Geographic Region In
The United States. 55th Annual Meeting of the American Society of Hematology. New Orleans,
LA; Dec 7-10, 2013. Blood 122(21); 995. http://bloodjournal.hematologylibrary.org/content/12
2/21/995.abstract.
Wang ZJ, Wood JC, Walter PB, Schoennagel BP, Evans P, Neumayr LD, Weyhmiller MG,
Harmatz P, Moon JC, Yuan Q, Miller JL, Weiss G, Grosse R, Meerpohl J, Nielsen P, Vichinsky E,
Porter JB, Fischer R. Iron distribution assessed by MRI in sickle cell disease, thalassemia
and Diamond Blackfan Anemia (MCSIO Pilot Study). International BioIron Society Meeting.
University College London; April 14-18, 2013.
Weisdorf DJ, Guethlein LA, Klein JP, Wang T, Marsh SGE, Spellman S, Haagenson MD, Saeturn
K, Ladner M, Trachtenberg E, Parham P, Miller JS. Recipient HLA-C1 Enhances The Clinical
Advantage Of Killer-Cell Immunoglobulin-Like Receptor B haplotype Donors In
Myeloablative Unrelated Transplantation For Acute Myelogenous Leukemia. 54th Annual
Meeting of the American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood
122(21); 549. http://bloodjournal.hematologylibrary.org/content/12 2/21/549.abstract.
Wun T, Telen MJ, Krishnamurti L, McCavit TL, DeCastro LM, Flanner H, Kuypers FA, Larkin SK,
Rhee S, Magnani JL, Thackray HM. Pan-Selectin Antagonist Rivipansel (GMI-1070) Reduces
Soluble E-Selectin Levels While Improving Clinical Outcomes in SCD Vaso-Occlusive
Crisis. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood
124(21); 2704. http://www.bloodjournal.org/content/124/21/2704.
Yang E, Baltz B, Adams-Graves P, Paley C, Esposito B, Vichinsky E. 12-month follow-up for
patients with sickle cell disease in an ongoing 3-year prospective, non-interventional
registry trial. SCDAA 41st Annual Convention; Sept 25-27, 2013. Baltimore, MD.
Yesim A, Galanello R, Viprakasit V, Piga A, Harmatz P, Forni GL, Shah F, Grace R, Porter J,
Vichinsky E, Wood J, Krishnan S, Zhang P, Abi-Saab W, Rienhoff HY, Neufeld E. The safety,
tolerability and efficacy of FBS0701, an iron chelator in clinical development for
transfusional iron overload: Data from 72 weeks of treatment. 18th Congress of the
European Hematology Association. Stockholm, Sweden; June 13-16, 2013.